Glycogen Storage Disease - 119 Studies Found
Recruiting |
: A Natural History Study of Adult Onset Pompe Disease Using Muscle MRI : Pompe Disease : 2013-07-31 |
Completed |
: Albuterol in Individuals With Late Onset Pompe Disease (LOPD) : Pompe Disease : 2013-05-08 : Drug: Albuterol Albuterol 4 mg |
Completed |
: Safety and Efficacy of Albuterol on Motor Function in Individuals With Late-onset Pompe Disease Receiving Enzyme Replacement Therapy : Pompe Disease : 2013-06-21 :
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Recruiting |
: Muscle Response to Enzyme Replacement Therapy in Pompe Disease : Pompe Disease : 2008-07-09 |
Recruiting |
: Response to Diaphragmatic Pacing in Subjects With Pompe Disease : Pompe Disease : 2015-01-21 :
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Recruiting |
: Observational Study for Subjects With Pompe Disease Undergoing Immune Modulation Therapies : Pompe Disease : 2011-09-15 :
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Recruiting |
: Pompe Disease Registry :
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Completed |
: Safety Study of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase to Treat Pompe Disease : Pompe Disease : 2009-07-13 :
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Withdrawn |
: High Protein and Exercise Therapy Plus Nocturnal Enteral Feeding in Juvenile-onset Pompe Disease : Glycogen Storage Disease Type II : 2012-08-01 : Other: High Protein and Exercise Therapy along-with Nocturnal Enteral Feeding |
Not yet recruiting |
: Re-administration of Intramuscular AAV9 in Patients With Late-Onset Pompe Disease : Pompe Disease : 2014-09-11 :
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