Search for Clinical Trial Results
Mucopolysaccharidosis Type I - 128 Studies Found
Status | Study |
Completed |
Study Name: Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B) Condition: Sanfilippo Syndrome Type B Date: 2012-01-10 |
Completed |
Study Name: Neurobehavioral Phenotypes in MPS III Condition:
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Recruiting |
Study Name: A Treatment Study of Mucopolysaccharidosis Type IIIB Condition:
Date: 2016-02-27 Interventions: Drug: BMN 250 Chimeric fusion of recombinant human alpha-N-acetylglucosaminidase and truncated human ins |
Completed |
Study Name: Safety, Tolerability, Ascending Dose and Dose Frequency Study of rhHNS Via an IDDD in MPS IIIA Patients Condition: Sanfilippo Syndrome Type A (MPS IIIA) Date: 2010-06-24 Interventions:
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Recruiting |
Study Name: Biomarker for Sanfilippo Disease Condition:
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Completed |
Study Name: Randomized, Controlled, Open-label, Multicenter, Safety and Efficacy Study of rhHNS Administration Via an IDDD in Pediatric Patients With Early Stage MPS IIIA Disease Condition: Sanfilippo Syndrome Date: 2014-02-10 Interventions: Drug: Recombinant human heparan N-sulfatase [rhHNS] Recombinant human heparan N-sulfatase [rhHNS] |
Completed |
Study Name: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB Condition: MPS IIIB (Sanfilippo Syndrome) Date: 2014-11-03 |
Completed |
Study Name: Natural History Studies of Mucopolysaccharidosis III Condition:
Date: 2013-11-26 Interventions:
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Recruiting |
Study Name: Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH for Mucopolysaccharidosis (MPS) IIIA Condition: Mucopolysaccharidosis Type 3 A Sanfilippo Syndrome Date: 2016-03-17 Interventions: Biological: scAAV9.U1a.hSGSH Self-complementary adeno-associated virus serotype 9 carrying the human SGS |
Enrolling by invitation |
Study Name: An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093. Condition:
Date: 2015-01-21 Interventions: Drug: HGT-1410 HGT-1410 administered according to Patient Group assignment. |