Gangliosidoses - 36 Studies Found
Completed |
: Stem Cell Transplant for Inborn Errors of Metabolism :
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Completed |
: Gene Therapy for Tay-Sachs Disease :
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Active, not recruiting |
: Efficacy Study of an Online Educational Module Before Carrier Genetic Screening in Persons of Ashkenazi Jewish Descent. :
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Completed |
: Diagnostic and Screening Study of Genetic Disorders :
|
Recruiting |
: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells :
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Active, not recruiting |
: Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders :
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Completed |
: Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders :
: 2012-06-20 :
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Withdrawn |
: Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases :
: 2009-10-20 : Biological: ALD-601 ALD-601 is manufactured by Aldagen from the 20% compartment of the selected umbilica |
Terminated |
: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases :
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Completed |
: Pyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease) :
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