Search for Clinical Trial Results

Limb-girdle Muscular Dystrophy Type 2A - 11 Studies Found
Status | Study |
Recruiting |
Study Name: A Trial of PF-06252616 in Ambulatory Participants With LGMD2I Condition: LGMD2I Date: 2016-07-12 Interventions: Drug: PF 06252616 |
Enrolling by invitation |
Study Name: Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA Condition: Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) Date: 2013-07-24 Interventions: Drug: scAAVrh74.tMCK.hSGCA |
Completed |
Study Name: Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I Condition:
|
Completed |
Study Name: Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C Condition:
|
Completed |
Study Name: Deflazacort in Dysferlinopathies Condition:
|
Completed |
Study Name: Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) Condition: Muscular Dystrophies Date: 2007-06-27 Interventions:
|
Completed |
Study Name: MRI on Persons With Mutations in POMT2 Gene (LGMD2N) Condition: Limb-girdle Muscular Dystrophy Date: 2016-04-27 |
Active, not recruiting |
Study Name: Clinical Outcome Study for Dysferlinopathy Condition:
|
Recruiting |
Study Name: Congenital Muscle Disease Study of Patient and Family Reported Medical Information Condition:
|
Completed |
Study Name: The Safety and Biological Activity of ATYR1940 in Patients With Limb Girdle or Facioscapulohumeral Muscular Dystrophies Condition:
Date: 2015-09-28 Interventions:
|